Find participating medical centers and current study status in each of them

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    A clinical trial to look at how risdiplam is processed by the body and how safe it is in treatment of very young babies with spinal muscular atrophy

    A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy

    • Muscle And Peripheral Nerve Disease
    • Spinal Muscular Atrophy (SMA)